HNF is advancing and supporting clinical research and trials for CMT.
HNF has been instrumental in advancing and supporting clinical trials by providing valuable patient insight, innovative data collection, and regulatory initiatives to assist in industry-sponsored clinical trial design and to inform the FDA for decision-making and oversight during drug development and commercialization of drugs and gene therapies for CMT.
Learn about clinical trials and how you can participate.
Without your participation, researchers won’t have the essential patient information to develop drugs, gene therapies, and clinical trials for Charcot-Marie-Tooth and other Inherited Neuropathies. In addition, as GRIN grows, we gain greater insights from you as patients to help accelerate therapies for Charcot-Marie-Tooth (CMT) and Inherited Neuropathies.
CMT Thrive Webinar:
The Key Role CMT Patients Play in Research
Presented by: Joy Aldrich, HNF GRIN Patient Registry Coordinator
Learn more on this topic
Latest News and Related Blog Posts
Webinar Recording: Why CMT Biomarkers Can’t Wait
Webinar Recording: Why CMT Biomarkers Can’t Wait Thank you to everyone who joined HNF’s live webinar, Why Biomarkers Can’t Wait, focused on the urgent need to develop meaningful, regulatory-ready biomarkers for Charcot–Marie–Tooth, (CMT). HNF leadership and leading...
HNF TRIAD Partner: A note to the CMT community from NMD Pharma
With gratitude and respect: a note to the CMT community from NMD Pharma Dear members of the CMT patient and caregiver community, We wanted to take a moment to communicate with you directly, following our recent press release announcement about ignaseclant (previously...
Allison Moore Receives Award for Community Impact in Research
Muscular Dystrophy Association’s Legacy Awards Honor Innovators in Clinical and Scientific Research, and Community Impact at the 2026 MDA Clinical & Scientific Conference in March MDA Legacy Award for Achievement in Clinical Research to honor Michio Hirano, MD,...
The Nerve to Cure Event, Columbia Missouri
Join us Saturday, October 4th from 12pm – 8pm October 4, 2025
The Nerve to Cure
CMT Social + Science Day with Evening Fundraiser Dinner
Big News for the CMT-SORD Community
Big News for the CMT-SORD Community Updates from HNF’s TRIAD Partner, Applied Therapeutics In a newly released press release, Applied Therapeutics—a valued HNF TRIAD partner—shared exciting progress in the development of treatments and diagnostics for CMT-SORD, a rare...
GRIN is Changing the Game for CMT Research
6,000+ Strong Across 72 Countries — 2025 GRIN is Changing the Game for CMT Research! We’re thrilled to announce a major milestone: Over 6,000 GRIN members from 72 countries have joined forces to advance research for Charcot-Marie-Tooth (CMT) and Inherited Neuropathies...
First Humans Dosed in New CMT Drug Trial
A New CMT Treatment Is One Step Closer Augustine Therapeutics Begins Phase I Trial of AGT‑100216 Exciting news for the CMT community! TRIAD partner, Augustine Therapeutics has officially dosed the first human participant in their Phase I clinical trial of AGT‑100216—a...
7 Reasons You Can’t Miss the Nashville CMT Summit
Mark your calendars for April 24–26, 2025, because the Nashville CMT Summit is bringing the ultimate blend of knowledge, community, and fun! Here are 7 reasons you absolutely need to be there: Test & Try Mobility Aids: Explore the latest tools to keep you moving...
Dr. Kayla Cornett to Present Groundbreaking CMT Wearable Sensor Study at MDA Clinical and Scientific Conference
On March 19th, at the MDA Clinical and Scientific Conference in Dallas, TX, Dr. Cornett will present exciting findings from the wearable sensor study conducted in collaboration with HNF’s partner, BioSensics. This innovative research highlights the potential of...
CMT Summit + Retreat 2025
CMT Summit + Retreat 2025: Uniting Patients, Researchers, Regulators, and Industry Leaders to Accelerate CMT Research Join patients, researchers, and industry leaders April 24-26 in Nashville to advance CMT research and empower wellness. The Hereditary Neuropathy...